Rare diseases treatment availability rate

Approximately 7,000 rare diseases exist today yet only 5% have an available treatment.

The figure above was extracted from this passage. If it does not match, the extraction is wrong and we want to know.

Published under CC BY 4.0. Attribute the original publisher; the citations below do that for you and link to this permanent record.

APA

PhRMA. (2025). Research & Development. Retrieved September 17, 2026, from https://phrma.org/policy-issues/research-development. Via StatOrigin, https://statorigin.org/stat/stat_3G0PECR75YC670M97PDAEJET36

Copy

MLA

PhRMA. "Research & Development." 2025, https://phrma.org/policy-issues/research-development. Accessed 17 Sept. 2026 via StatOrigin, https://statorigin.org/stat/stat_3G0PECR75YC670M97PDAEJET36.

Copy

Chicago

PhRMA. "Research & Development." 2025. https://phrma.org/policy-issues/research-development. Accessed September 17, 2026. Cited from StatOrigin, https://statorigin.org/stat/stat_3G0PECR75YC670M97PDAEJET36.

Copy

BibTeX

@misc{phrma2025rareejet36, author = {{PhRMA}}, title = {Research \& Development}, year = {2025}, howpublished = {StatOrigin, https://statorigin.org}, url = {https://statorigin.org/stat/stat_3G0PECR75YC670M97PDAEJET36}, note = {Original source: https://phrma.org/policy-issues/research-development. Accessed September 17, 2026.} }

Copy

Everything needed to check this number yourself, without taking our word for it.

Record last modified 17 September 2026. Value type: estimate. Update cadence: irregular. This page is permanently addressable at statorigin.org/stat/stat_3G0PECR75YC670M97PDAEJET36.