Orphan drug approvals

Number of therapies targeting rare diseases approved after receiving an orphan drug designation.

Unit Count Industry Pharmaceuticals

Records
1
Regions
1
Period
2024
Sources
1
Verification 1 verified data points Verified 17 Sep 2026 Next update Sources typically refresh annually

The chart

The figure

One published observation so far. A chart follows as soon as a second period is published.

Orphan drug approvals

United States, 2024

1 observation
26 United States · 2024 · FDA · full record
Source: FDA · CC BY 4.0 · statorigin.org

Every record

All records

1 record · 1 region · 2024

Orphan drug approvals: every record, grouped by region, newest first.
Period Value Source Type
United States 1 record
2024 26 FDA · 31 Dec 2024 actual

Primary documents

Sources

1 document. Each links to the publisher's own copy.

Cite & reuse

Cite this page

Data on this page is published under CC BY 4.0. You may reuse it, including commercially, provided you attribute it. To cite one figure, open its record: each carries APA, MLA, Chicago and BibTeX forms that credit the original publisher.

StatOrigin. (2026). Orphan drug approvals. Retrieved from https://statorigin.org/indicators/orphan-drug-approvals